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Bone Marrow Failure Disorders

Inherited or acquired diseases characterized by insufficient and/or dysplastic blood cells.

Subtype terms (2)

More specific conditions that are subtypes of Bone Marrow Failure Disorders in the MeSH hierarchy.

  • Anemia, Aplastic

    105 drugs (64 approved, 41 experimental)

  • Congenital Bone Marrow Failure Syndromes

    10 drugs (9 approved, 1 experimental)

Drugs by status

Phase 3 trials (5)

  • cyclophosphamide
  • Anti-thymocyte Globulin (Rabbit)
  • fludarabine
  • methadone
  • morphine

Phase 2 trials (36)

  • methylprednisolone
  • plerixafor
  • busulfan
  • clofarabine
  • prednisone
  • eltrombopag
  • tacrolimus
  • lymphocyte immune globulin, anti-thymocyte globulin (equine)
  • hemopoietic stem cell
  • bone marrow derived mesenchymal stem cells
  • haploidentical mononuclear cells
  • hydroxyurea
  • Filgrastim
  • pembrolizumab
  • levamisole
  • ibrutinib
  • sirolimus
  • cyclosporine
  • mycophenolate
  • t cell depleted hematopoietic stem cells
  • alemtuzumab
  • nandrolone phenpropionate
  • allogeneic cord blood
  • autologous cd34+ cells
  • autologous umbilical cord blood
  • umbilical cord mesenchymal stem cells
  • cd45-depleted allogenic peripheral blood stem cell
  • mesna
  • methotrexate
  • rituximab
  • +6 more

Phase 1 trials (7)

  • thymidine
  • deoxycytidine
  • romiplostim
  • aldhbr umbilical cord blood cells
  • cd7 car-t cell
  • exg34217
  • doxecitine

Other trials (2)

  • alefacept
  • um-171

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