← All indications
Hemoglobinopathies
A group of inherited disorders characterized by structural alterations within the hemoglobin molecule.
Subtype terms (3)
More specific conditions that are subtypes of Hemoglobinopathies in the MeSH hierarchy.
- Anemia, Sickle Cell
293 drugs (178 approved, 115 experimental)
- Hemoglobin C Disease
- Thalassemia
65 drugs (48 approved, 17 experimental)
Drugs by status
Phase 4 trials (3)
Phase 3 trials (3)
Phase 2 trials (24)
- thalidomide
- bpx-501
- busulfan
- pyridoxal isonicotinoyl hydrazone
- clofarabine
- deferoxamine
- prednisone
- tacrolimus
- sirolimus
- cyclosporine
- mycophenolate
- cyclophosphamide
- stem cells
- alemtuzumab
- Anti-thymocyte Globulin (Rabbit)
- allogeneic cord blood
- fludarabine
- thiotepa
- sargramostim
- melphalan
- phenytoin
- treosulfan
- herv-e tcr transduced cd8+/cd34+ t cells in hlaa* 11:01 positive patients
- EDIT-301
Phase 1 trials (7)
Organizations
Organization Involved with Phase 4 Indications (2)
Organization Involved with Phase 3 Indications (24)
- National Heart, Lung, and Blood Institute (NHLBI)
- National Marrow Donor Program
- Consorzio per Valutazioni Biologiche e Farmacologiche
- Duke University
- Hoosier Cancer Research Network
- Johns Hopkins University
- University of Kansas
- University of Miami
- Columbia University
- East Carolina University
- University of Cincinnati
- Icahn School of Medicine at Mount Sinai
- University of Minnesota
- Ospedali Riuniti Villa Sofia-Cervello
- State University of New York, Brooklyn
- University of Mississippi
- Washington University in St. Louis
- University of Illinois at Chicago
- George Washington University
- Maryland Medical Research Institute
- Gamble Institute of Medical Research
- European Commission
- The University of Texas, Dallas
- St. Jude Children's Hospital
Organization Involved with Phase 2 Indications (34)
- Vertex
- Bellicum Pharmaceuticals
- INC Research
- Sponsor GmbH
- Gamida Cell
- National Institutes of Health (NIH)
- National Institute of Allergy and Infectious Diseases (NIAID)
- National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)
- University of Roma La Sapienza
- University of Pennsylvania
- Baylor University
- Case Western Reserve University
- Harvard University
- Emory University
- Temple University
- Gottfried Wilhelm Leibniz Universität Hannover
- Hahnemann University Hospital
- Northwell Health
- Ohio State University
- University of Florida
- University of Louisville
- University of Bari
- Leiden University
- Celerion
- Hôpital universitaire Robert-Debré
- Louisiana State University
- Pierrel Research
- Steven & Alexandra Cohen Children's Medical Center, New York
- Methodist Cancer Center, Houston, Texas
- Children's National Medical Center
- +4 more
Organization Involved with Phase 1 Indications (7)
Organization Involved with Other Experimental Indications (1)