Osteopetrosis

Approved for this indication (1)

• interferon gamma-1b

Phase 3 trials (11)

• busulfan
• somatropin
• naltrexone
• cyclosporine
• cyclophosphamide
• stem cells
• alemtuzumab
• calcitriol
• autologous umbilical cord blood
• allogeneic bone marrow
• fludarabine

Phase 2 trials (8)

• acetylcysteine
• bpx-501
• clofarabine
• tacrolimus
• celecoxib
• allogeneic cord blood
• humulus lupulus
• interferon beta-1b

Phase 1 trials (2)

• parathyroid hormone
• rp-l401

Other trials (4)

• muromonab cd3
• autologous cd34+ cells
• thiotepa
• melphalan

Organization Involved with Phase 3 Indications (5)

• Columbia University
• Medical University of South Carolina
• Food and Drug Administration
• University of Minnesota
• Isfahan University

Organization Involved with Phase 2 Indications (6)

• Horizon Pharma
• Bellicum Pharmaceuticals
• Indiana University
• Los Angeles Biomedical Research Institute
• University of California, Los Angeles
• Children's Hospital Los Angeles

Organization Involved with Phase 1 Indications (2)

• University of Chicago
• Rocket Pharma Limited

Organization Involved with Other Experimental Indications (2)

• University of California, San Francisco
• St. Jude Children's Hospital