← Mechanisms of action
HTT
SINGLE PROTEINHomo sapiens
Preferred name: Huntingtin ChEMBL ↗
Linked proteins
Drugs acting on this target (11)
| Active Pharmaceutical Ingredient | Mechanism Type ▲ | Approval Status | API Type | Mechanism of Action |
|---|---|---|---|---|
| aln-htt02 | Antisense inhibitor | experimental | Nucleic acid | HTT antisense inhibitor |
| raav5-mihtt | Antisense inhibitor | experimental | Gene therapy | HTT antisense inhibitor |
| sky-0515 | Antisense inhibitor | experimental | Nucleic acid | HTT antisense inhibitor |
| VY-HTT01 | Antisense inhibitor | experimental | Gene therapy | HTT antisense inhibitor |
| wve-003 | Antisense inhibitor | experimental | Nucleic acid | HTT antisense inhibitor |
| wve-120101 | Antisense inhibitor | experimental | Nucleic acid | HTT antisense inhibitor |
| ptc518 | Inhibitor | experimental | Small molecule | HTT inhibitor |
| ro7234292 | Inhibitor | experimental | mAb | HTT inhibitor |
| wve-120102 | Inhibitor | experimental | Nucleic acid | HTT inhibitor |
| ionis httrx | Rnai inhibitor | experimental | Nucleic acid | HTT rnai inhibitor |
| autologous cd133+ stem cells | Tissue restoration | experimental | Cell therapy | HTT tissue restoration |