raav5-mihtt
Gene therapyexperimental
Clinical trial activity
2 trials · 1 clinical orgs · 0 marketing orgs
Phase 1
2
Phase 2
2
Phase 3
0
Phase 4
0
Earliest trial started Oct 31, 2019 (NCT04120493)
Timeline
2010s
- Jan 1, 2019
Earliest Phase 1 Sponsor(trial)
Indications
Studied for
Mechanism of action
- HuntingtinANTISENSE INHIBITOR
HTT antisense inhibitor
Chemistry & pharmacology
Oral
No
Parenteral
No
Topical
No
Clinical trials
| NCT ID | Phase | Start date | Sponsor(s) |
|---|---|---|---|
| NCT05243017 | Phase 1/Phase 2 (Phase 2) | Oct 7, 2021 | UniQure N.V. |
| NCT04120493 | Phase 1/Phase 2 (Phase 2) | Oct 31, 2019 | UniQure N.V. |
Showing 2 of 2 trials
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Organizations
Research & Development (1)
| Organization | Org type | Trials | As lead sponsor | Phases | Earliest year |
|---|---|---|---|---|---|
| UniQure N.V. | For profit | 2 | 2 | 1 | 2019 |
1 organizations
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