Heredodegenerative Disorders, Nervous System
Inherited disorders characterized by progressive atrophy and dysfunction of anatomically or physiologically related neurologic systems.
Subtype terms (26)
More specific conditions that are subtypes of Heredodegenerative Disorders, Nervous System in the MeSH hierarchy.
- Alexander Disease
1 drug experimental
- Amyloid Neuropathies, Familial
10 drugs (7 approved, 3 experimental)
- Bulbo-Spinal Atrophy, X-Linked
8 drugs (4 approved, 4 experimental)
- Canavan Disease
7 drugs (3 approved, 4 experimental)
- Cockayne Syndrome
1 drug approved
- Dystonia Musculorum Deformans
- Gerstmann-Straussler-Scheinker Disease
- Hepatolenticular Degeneration
23 drugs (11 approved, 12 experimental)
- Hereditary Central Nervous System Demyelinating Diseases
- Hereditary Sensory and Autonomic Neuropathies
3 drugs (2 approved, 1 experimental)
- Hereditary Sensory and Motor Neuropathy
4 drugs (2 approved, 2 experimental)
- Huntington Disease
97 drugs (44 approved, 53 experimental)
- Lafora Disease
2 drugs experimental
- Myotonia Congenita
4 drugs approved
- Myotonic Dystrophy
18 drugs (8 approved, 10 experimental)
- Neuroacanthocytosis
- Neurofibromatoses
21 drugs (17 approved, 4 experimental)
- Neuronal Ceroid-Lipofuscinoses
18 drugs (6 approved, 12 experimental)
- Optic Atrophies, Hereditary
1 drug experimental
- Pantothenate Kinase-Associated Neurodegeneration
2 drugs (1 approved, 1 experimental)
- Spinal Muscular Atrophies of Childhood
14 drugs (9 approved, 5 experimental)
- Spinocerebellar Degenerations
5 drugs (2 approved, 3 experimental)
- Tourette Syndrome
49 drugs (31 approved, 18 experimental)
- Tuberous Sclerosis
16 drugs (11 approved, 5 experimental)
- Unverricht-Lundborg Syndrome
3 drugs approved
- X-Linked Intellectual Disability
1 drug approved
Drugs by status
Phase 3 trials (1)
Phase 2 trials (3)
Organizations
Organization Involved with Phase 2 Indications (1)