berotralstat

Trade name: Orladeyo

Small moleculeapprovedOrphan Drug FDAFast Track FDA

Approved

Dec 3, 2020

Clinical trial activity

12 trials · 10 clinical orgs · 1 marketing orgs

Phase 1
4
Phase 2
6
Phase 3
5
Phase 4
0

Earliest trial started May 1, 2015 (NCT02448264)

Timeline

2010s

  1. Jan 1, 2015

    BioCryst — Earliest Phase 1 Sponsor(trial)

  2. Jan 1, 2016

    BioCryst — Earliest Phase 2 Sponsor(trial)

  3. Nov 1, 2017

    Orphan Drug Designation

  4. Jan 1, 2018

    BioCryst — Earliest Phase 3 Sponsor(trial)

2020s

  1. Dec 3, 2020

    BioCryst — Earliest FDA Approval

  2. Dec 3, 2020

    BioCryst — Marketing Organization

  3. Dec 3, 2020

    BioCryst — NDA Secondary Org

  4. Dec 3, 2020

    BioCryst — NDA Organization

Indications

Mechanism of action

Approval history

  • approvedFast trackDec 3, 2020

Chemistry & pharmacology

Loading structure…

SMILES

N#Cc1cccc(C(NCC2CC2)c2ccc(F)c(NC(=O)c3cc(C(F)(F)F)nn3-c3cccc(CN)c3)c2)c1
Mol. weight
562.57 g/mol
Lipinski Ro5
2 violation(s)
Rule of 3
No
Chirality
Single Stereoisomer
Inorganic
No
Polymer
No
Delivery
Oral
Availability
Prescription Only

Oral

Yes

Parenteral

No

Topical

No

Sources

Also known as

  • bcx7353

Clinical trials

NCT IDPhaseStart dateSponsor(s)
NCT05453968Phase 3Oct 25, 2022BioCryst, University of Bristol
NCT04933721Phase 3Jun 30, 2021BioCryst, PHI University
NCT03873116Phase 3Feb 28, 2019BioCryst, Saiyu Soka Hospital
NCT03472040Phase 2/Phase 3 (Phase 3)Feb 16, 2018BioCryst, Semmelweis University
NCT03485911Phase 3Feb 6, 2018BioCryst, University of California, San Diego
NCT03240133Phase 2Jul 31, 2017Barts & The London NHS Trust, BioCryst
NCT03202784Phase 1Feb 27, 2017BioCryst, Quotient
NCT03136237Phase 1Feb 17, 2017BioCryst, Covance
NCT02870972Phase 2Aug 1, 2016BioCryst, J. W. Goethe University
NCT02819102Phase 1Mar 1, 2016BioCryst, Quotient
NCT02448264Phase 1May 1, 2015BioCryst, Quotient
NCT04428632N/ABioCryst
Showing 12 of 12 trials
Page 1 / 1

Organizations

Research & Development (10)

OrganizationOrg typeTrialsAs lead sponsorPhasesEarliest year
BioCrystFor profit121242015
QuotientFor profit3012015
Barts & The London NHS TrustAcademic/Hospital1012017
CovanceFor profit1012017
J. W. Goethe UniversityAcademic/Hospital1012016
PHI UniversityAcademic/Hospital1012021
Saiyu Soka HospitalAcademic/Hospital1012019
Semmelweis UniversityAcademic/Hospital1012018
University of BristolAcademic/Hospital1012022
University of California, San DiegoAcademic/Hospital1012018
10 organizations
Page 1 / 1

Marketing (4)

OrganizationOrg typeRelationshipDate
BioCrystFor profitSYNDec 3, 2020
BioCrystFor profitMKTGDec 3, 2020
BioCrystFor profitNDA2Dec 3, 2020
BioCrystFor profitNDADec 3, 2020