cedazuridine

Trade name: Inqovi

Small moleculeapprovedOrphan Drug FDA

Approved

Jul 7, 2020

Clinical trial activity

66 trials · 44 clinical orgs · 2 marketing orgs

Phase 1
44
Phase 2
38
Phase 3
3
Phase 4
0

Earliest trial started May 1, 2014 (NCT02103478)

Timeline

2010s

  1. Jan 1, 2014

    Earliest Phase 1 Sponsor(trial)

  2. Jan 1, 2018

    Earliest Phase 3 Sponsor(trial)

  3. Jan 1, 2019

    Earliest Phase 2 Sponsor(trial)

  4. Aug 21, 2019

    Orphan Drug Designation

2020s

  1. Jul 7, 2020

    Otsuka — Earliest FDA Approval

  2. Jul 7, 2020

    Otsuka — NDA Secondary Org

  3. Jul 7, 2020

    Otsuka — NDA Organization

  4. Jul 7, 2020

    Taiho Pharmaceutical — NDA Secondary Org

Indications

Mechanism of action

Combination products

  • inqovi

    with decitabine

    Also known as decitabine and cedazuridine

Approval history

  • approvedPriority reviewJul 7, 2020

Chemistry & pharmacology

Loading structure…

SMILES

O=C1N[C@H](O)CCN1[C@@H]1O[C@H](CO)[C@@H](O)C1(F)F
Mol. weight
268.22 g/mol
Lipinski Ro5
Pass
Rule of 3
No
Chirality
Single Stereoisomer
Inorganic
No
Polymer
No
Delivery
Oral
Availability
Prescription Only

Oral

Yes

Parenteral

No

Topical

No

Sources

Also known as

  • astx727

Clinical trials

NCT IDPhaseStart dateSponsor(s)
NCT07153497Phase 2Feb 26, 2026National Cancer Institute (NCI)
NCT07148947Phase 2Feb 1, 2026Swedish Orphan Biovitrum, University of Washington
NCT07012044Phase 1Oct 31, 2025National Cancer Institute (NCI)
NCT06802523Phase 1Apr 30, 2025National Cancer Institute (NCI), Yale University
NCT06597734Phase 2Mar 11, 2025Rigel Pharmaceuticals, University of Texas at Houston
NCT06802146Early Phase 1 (Phase 1)Feb 7, 2025Astex Pharmaceuticals, Inc., Breakthrough Cancer Research, Harvard University
NCT06672146Phase 2Feb 3, 2025National Cancer Institute (NCI), SWOG Cancer Research Network
NCT06661915Phase 2Jan 31, 2025City of Hope National Medical Center, National Cancer Institute (NCI)
NCT06284460Phase 1/Phase 2 (Phase 2)Jan 31, 2025University of Texas at Houston
NCT06577441Phase 2Jan 17, 2025National Cancer Institute (NCI)
NCT06484062Phase 1Dec 6, 2024Harvard University, National Cancer Institute (NCI)
NCT06297629Phase 2Jul 1, 2024Astex Pharmaceuticals, Inc., University of Texas at Houston
NCT06357858Phase 1Jun 1, 2024Case Western Reserve University
NCT06113289Phase 1/Phase 2 (Phase 2)Apr 1, 2024University of Texas at Houston
NCT06177171Phase 1Apr 1, 2024National Cancer Institute (NCI), University of California, San Francisco
NCT06327685Phase 1Mar 13, 2024Blueprint Medicines Corporation, University of South Florida
NCT06191978Phase 1Mar 7, 2024Astex Pharmaceuticals, Inc., University of Texas at Houston
NCT06351306Phase 2Jan 30, 2024Columbia University
NCT05960773Phase 2Jan 3, 2024National Cancer Institute (NCI)
NCT05799079Phase 2Dec 31, 2023National Comprehensive Cancer Network, Otsuka, Vanderbilt University
Showing 20 of 66 trials
Page 1 / 4

Organizations

Research & Development (44)

OrganizationOrg typeTrialsAs lead sponsorPhasesEarliest year
Astex Pharmaceuticals, Inc.For profit271332014
National Cancer Institute (NCI)Government171422021
University of Texas at HoustonAcademic/Hospital131322021
OtsukaFor profit7332019
Harvard UniversityAcademic/Hospital5312019
National Comprehensive Cancer NetworkAcademic/Hospital3022021
Vanderbilt UniversityAcademic/Hospital3312019
Yale UniversityAcademic/Hospital3022021
GenentechFor profit2022021
Australian National UniversityAcademic/Hospital1012022
Blueprint Medicines CorporationFor profit1012024
Breakthrough Cancer ResearchAcademic/Hospital1012025
Case Western Reserve UniversityAcademic/Hospital1112024
Chiltern InternationalFor profit1012018
City of Hope National Medical CenterAcademic/Hospital1012025
Clinical Hub for Interventional Research (CHOIR)Academic/Hospital1112022
Columbia UniversityAcademic/Hospital1112024
Forma Therapeutics, Inc.For profit1012019
Groupe Francophone des MyelodysplasiesAcademic/Hospital1112021
Imperial College LondonAcademic/Hospital1112022
44 organizations
Page 1 / 3

Marketing (3)

OrganizationOrg typeRelationshipDate
OtsukaFor profitNDA2Jul 7, 2020
OtsukaFor profitNDAJul 7, 2020
Taiho PharmaceuticalFor profitNDA2Jul 7, 2020