resmetirom

Trade name: REZDIFFRA

Small moleculeapprovedFast Track FDABreakthrough Therapy FDA

Approved

Mar 14, 2024

Clinical trial activity

7 trials · 4 clinical orgs · 1 marketing orgs

Phase 1
2
Phase 2
4
Phase 3
3
Phase 4
1

Earliest trial started Dec 31, 2019 (NCT04197479)

Timeline

2010s

  1. Jan 1, 2019

    Madrigal Pharmaceuticals — Earliest Phase 3 Sponsor(trial)

2020s

  1. Jan 1, 2024

    Madrigal Pharmaceuticals — Earliest Phase 1 Sponsor(trial)

  2. Mar 14, 2024

    Madrigal Pharmaceuticals — Earliest FDA Approval

  3. Mar 14, 2024

    Madrigal Pharmaceuticals — NDA Organization

  4. Jan 1, 2026

    Earliest Phase 2 Sponsor(trial)

Indications

Mechanism of action

Approval history

  • approvedPriority reviewAcceleratedFast trackBreakthroughMar 14, 2024

Chemistry & pharmacology

Oral

No

Parenteral

No

Topical

No

Clinical trials

NCT IDPhaseStart dateSponsor(s)
NCT07143968Phase 2Jan 31, 2026Indiana University
NCT07249788Phase 4Nov 30, 2025Nabiqasim Industries (Pvt) Ltd
NCT07216313Phase 1Sep 30, 2025Sagimet Biosciences Inc.
NCT06397872Phase 1Mar 5, 2024Madrigal Pharmaceuticals
NCT05500222Phase 3Aug 26, 2022Madrigal Pharmaceuticals
NCT04951219Phase 3Jul 9, 2021Madrigal Pharmaceuticals
NCT04197479Phase 3Dec 31, 2019Madrigal Pharmaceuticals
Showing 7 of 7 trials
Page 1 / 1

Organizations

Research & Development (4)

OrganizationOrg typeTrialsAs lead sponsorPhasesEarliest year
Madrigal PharmaceuticalsFor profit4422019
Indiana UniversityAcademic/Hospital1112026
Nabiqasim Industries (Pvt) LtdFor profit1112025
Sagimet Biosciences Inc.For profit1112025
4 organizations
Page 1 / 1

Marketing (1)

OrganizationOrg typeRelationshipDate
Madrigal PharmaceuticalsFor profitNDAMar 14, 2024