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Globotriosylceramide

SMALL MOLECULEHomo sapiens

Drugs acting on this target (3)

Active Pharmaceutical Ingredient Mechanism Type Approval Status API Type Mechanism of Action
agalsidase alfa (Replagal)Hydrolytic enzymeexperimentalRecombinant proteinGlobotriosylceramide
agalsidase beta (Fabrazyme)Hydrolytic enzymeapprovedRecombinant proteinGlobotriosylceramide hydrolytic enzyme
pegunigalsidase alfa (Elfabrio)Hydrolytic enzymeapprovedRecombinant proteinGlobotriosylceramide hydrolytic enzyme