← Mechanisms of action

GAA

SINGLE PROTEINHomo sapiens
Preferred name: Lysosomal alpha-glucosidase ChEMBL ↗

Linked proteins

Drugs acting on this target (8)

Active Pharmaceutical Ingredient Mechanism Type Approval Status API Type Mechanism of Action
miglitol (glyset)InhibitorapprovedSmall moleculeGAA inhibitor
duvoglustatStabiliserexperimentalSmall moleculeGAA stabiliser
ab-1009SupplementationexperimentalGene therapyGAA supplementation
alglucosidase alfa (myozyme)SupplementationapprovedRecombinant proteinGAA supplementation
crg003SupplementationexperimentalGene therapyGAA supplementation
dnl952SupplementationexperimentalRecombinant proteinGAA supplementation
gc301SupplementationexperimentalGene therapyGAA supplementation
Reveglucosidase alfaSupplementationexperimentalRecombinant proteinGAA supplementation