← Mechanisms of action
Survival motor neuron protein
SINGLE PROTEINHomo sapiens
Linked proteins
Drugs acting on this target (5)
| Active Pharmaceutical Ingredient | Mechanism Type ▲ | Approval Status | API Type | Mechanism of Action |
|---|---|---|---|---|
| risdiplam (Evrysdi) | Activator | approved | Small molecule | Survival motor neuron protein activator |
| onasemnogene abeparvovec (Zolgensma) | Agonist | approved | Gene therapy | Survival motor neuron protein agonist |
| onasemnogene abeparvovec (Zolgensma) | Exogenous gene | approved | Gene therapy | Survival motor neuron protein exogenous gene |
| exg001-307 | Modulator | experimental | Gene therapy | Survival motor neuron protein modulator |
| onasemnogene abeparvovec (Zolgensma) | Supplementation | approved | Gene therapy | SMN1 |