exg001-307
Gene therapyexperimental
Clinical trial activity
3 trials · 1 clinical orgs · 0 marketing orgs
Phase 1
3
Phase 2
1
Phase 3
0
Phase 4
0
Earliest trial started Jan 21, 2022 (NCT06576388)
Timeline
2020s
- Jan 1, 2022
Earliest Phase 1 Sponsor(trial)
Indications
Mechanism of action
- Survival motor neuron proteinMODULATOR
Survival motor neuron protein modulator
Chemistry & pharmacology
Oral
No
Parenteral
No
Topical
No
Clinical trials
| NCT ID | Phase | Start date | Sponsor(s) |
|---|---|---|---|
| NCT06888661 | Early Phase 1 (Phase 1) | Mar 10, 2025 | Government of China |
| NCT05614531 | Phase 1/Phase 2 (Phase 2) | Nov 1, 2022 | Government of China |
| NCT06576388 | Early Phase 1 (Phase 1) | Jan 21, 2022 | Government of China |
Showing 3 of 3 trials
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Organizations
Research & Development (1)
| Organization | Org type | Trials | As lead sponsor | Phases | Earliest year |
|---|---|---|---|---|---|
| Government of China | Government | 3 | 3 | 2 | 2022 |
1 organizations
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