← Mechanisms of action

5-aminolevulinate synthase mRNA

NUCLEIC-ACIDHomo sapiens

Drugs acting on this target (2)

Active Pharmaceutical Ingredient Mechanism Type Approval Status API Type Mechanism of Action
givosiran (Givlaari)DegraderapprovedNucleic acid5-aminolevulinate synthase mRNA degrader
givosiran (Givlaari)Rnai inhibitorapprovedNucleic acid5-aminolevulinate synthase mRNA RNAi inhibitor