cystic fibrosis transmembrane conductance regulator
Gene therapyexperimental
Cystic fibrosis transmembrane conductance regulator (CFTR) is a membrane protein and anion channel in vertebrates that is encoded by the CFTR gene. — Wikipedia
Clinical trial activity
1 trials · 2 clinical orgs · 0 marketing orgs
Phase 1
1
Phase 2
0
Phase 3
0
Phase 4
0
Earliest trial started Jun 1, 1995 (NCT00004806)
Timeline
1990s
- Jan 1, 1995
Earliest Phase 1 Sponsor(trial)
Indications
Studied for
Mechanism of action
- Cystic fibrosis transmembrane conductance regulatorSupplementation
CFTR supplementation
Chemistry & pharmacology
Oral
No
Parenteral
No
Topical
No
Sources
Also known as
- cystic fibrosis transmembrane conductance regulator
Clinical trials
| NCT ID | Phase | Start date | Sponsor(s) |
|---|---|---|---|
| NCT00004806 | Phase 1 | Jun 1, 1995 | National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK), University of Alabama, Birmingham |
Showing 1 of 1 trials
Page 1 / 1
Organizations
Research & Development (2)
| Organization | Org type | Trials | As lead sponsor | Phases | Earliest year |
|---|---|---|---|---|---|
| National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK) | Government | 1 | 0 | 1 | 1995 |
| University of Alabama, Birmingham | Academic/Hospital | 1 | 1 | 1 | 1995 |
2 organizations
Page 1 / 1