aav8-hfix19

Gene therapyexperimental

Clinical trial activity

1 trials · 5 clinical orgs · 0 marketing orgs

Phase 1
1
Phase 2
0
Phase 3
0
Phase 4
0

Earliest trial started Oct 1, 2012 (NCT01620801)

Timeline

2010s

  1. Jan 1, 2012

    Earliest Phase 1 Sponsor(trial)

Indications

Mechanism of action

Chemistry & pharmacology

Oral

No

Parenteral

No

Topical

No

Also known as

  • aav8-hfix19

Clinical trials

NCT IDPhaseStart dateSponsor(s)
NCT01620801Phase 1Oct 1, 2012Spark Therapeutics, Trinity College Dublin, University of Pennsylvania, University of Pittsburgh, University of Sydney
Showing 1 of 1 trials
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Organizations

Research & Development (5)

OrganizationOrg typeTrialsAs lead sponsorPhasesEarliest year
Spark TherapeuticsFor profit1112012
Trinity College DublinAcademic/Hospital1012012
University of PennsylvaniaAcademic/Hospital1012012
University of PittsburghAcademic/Hospital1012012
University of SydneyAcademic/Hospital1012012
5 organizations
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