fexinidazole

Small moleculeapprovedOrphan Drug FDA

Approved

Jul 16, 2021

Fexinidazole is a medication used to treat African trypanosomiasis caused by Trypanosoma brucei gambiense. It is effective against both first and second stage disease. It is taken by mouth. — Wikipedia

Clinical trial activity

13 trials · 9 clinical orgs · 2 marketing orgs

Phase 1
5
Phase 2
4
Phase 3
5
Phase 4
0

Earliest trial started Sep 1, 2009 (NCT00982904)

Timeline

2000s

  1. Jan 1, 2009

    Earliest Phase 1 Sponsor(trial)

2010s

  1. Jan 1, 2012

    Earliest Phase 2 Sponsor(trial)

  2. Jan 1, 2016

    Earliest Phase 3 Sponsor(trial)

  3. Apr 4, 2016

    Orphan Drug Designation

2020s

  1. Jul 16, 2021

    Sanofi-Aventis — Earliest FDA Approval

  2. Jul 16, 2021

    Sanofi — Marketing Organization

  3. Jul 16, 2021

    Sanofi-Aventis — NDA Secondary Org

  4. Jul 16, 2021

    Sanofi-Aventis — NDA Organization

Indications

Mechanism of action

  • Unspecified targetOTHER

    Cytotoxic

    Nitro pro-drug that is reduced to form cytotoxic species

    Potential in leishmaniasis and trypanosomiasis

  • UnclearUnclear

    Unclear unclear

Approval history

  • approvedPriority reviewJul 16, 2021

Chemistry & pharmacology

Loading structure…

SMILES

CSc1ccc(OCc2ncc([N+](=O)[O-])n2C)cc1
Mol. weight
279.32 g/mol
Lipinski Ro5
Pass
Rule of 3
No
Chirality
Achiral Molecule
Inorganic
No
Polymer
No
Delivery
Oral
Availability
Prescription Only

Oral

Yes

Parenteral

No

Topical

No

Sources

Also known as

  • fexinidazole
  • fexinidazole
  • fexinidazole
  • fexinidazole
  • fexinidazole
  • hoe 239

Clinical trials

NCT IDPhaseStart dateSponsor(s)
NCT05607173Phase 1Dec 31, 2022Sanofi
NCT03974178Phase 2/Phase 3 (Phase 3)Jun 30, 2019Drugs for Neglected Diseases Initiative, European and Developing Countries Clinical Trials Partnership (EDCTP), Makerere University
NCT03587766Phase 2Nov 13, 2017Drugs for Neglected Diseases Initiative, University of Barcelona
NCT03025789Phase 3Nov 1, 2016Drugs for Neglected Diseases Initiative, Sanofi
NCT02571062Phase 1Mar 1, 2015Drugs for Neglected Diseases Initiative
NCT02498782Phase 2Jul 1, 2014Drugs for Neglected Diseases Initiative, Oswaldo Cruz Foundation
NCT02184689Phase 2/Phase 3 (Phase 3)May 1, 2014Drugs for Neglected Diseases Initiative
NCT02169557Phase 2/Phase 3 (Phase 3)May 1, 2014Drugs for Neglected Diseases Initiative
NCT01980199Phase 2Nov 1, 2013Drugs for Neglected Diseases Initiative, University of Khartoum
NCT01685827Phase 2/Phase 3 (Phase 3)Nov 1, 2012Drugs for Neglected Diseases Initiative, HAT National Control Program in DRC
NCT01483170Phase 1Sep 1, 2011Drugs for Neglected Diseases Initiative, SGS Life Sciences
NCT01340157Phase 1Feb 1, 2011Drugs for Neglected Diseases Initiative, Sanofi, SGS Life Sciences
NCT00982904Phase 1Sep 1, 2009Drugs for Neglected Diseases Initiative, Sanofi, SGS Life Sciences
Showing 13 of 13 trials
Page 1 / 1

Organizations

Research & Development (9)

OrganizationOrg typeTrialsAs lead sponsorPhasesEarliest year
Drugs for Neglected Diseases InitiativeAcademic/Hospital121232009
SanofiFor profit4122009
SGS Life SciencesFor profit3012009
European and Developing Countries Clinical Trials Partnership (EDCTP)Academic/Hospital1012019
HAT National Control Program in DRCAcademic/Hospital1012012
Makerere UniversityAcademic/Hospital1012019
Oswaldo Cruz FoundationAcademic/Hospital1012014
University of BarcelonaAcademic/Hospital1012017
University of KhartoumAcademic/Hospital1012013
9 organizations
Page 1 / 1

Marketing (3)

OrganizationOrg typeRelationshipDate
SanofiFor profitMKTGJul 16, 2021
Sanofi-AventisFor profitNDA2Jul 16, 2021
Sanofi-AventisFor profitNDAJul 16, 2021