coagulation factor ix (Recombinant), Fc-fusion protein

Trade name: Alprolix

BiologicalapprovedOrphan Drug FDA

Approved

Mar 28, 2014

Factor IX, also known as Christmas factor, is one of the serine proteases involved in coagulation; it belongs to peptidase family S1. Deficiency of this protein causes haemophilia B. — Wikipedia

Clinical trial activity

7 trials · 6 clinical orgs · 1 marketing orgs

Phase 1
3
Phase 2
4
Phase 3
4
Phase 4
0

Earliest trial started Apr 1, 2008 (NCT00716716)

Timeline

2000s

  1. Jan 1, 2008

    Bioverativ Therapeutics Inc. — Earliest Phase 1 Sponsor(trial)

  2. Oct 30, 2008

    Orphan Drug Designation

  3. Jan 1, 2009

    Bioverativ Therapeutics Inc. — Earliest Phase 3 Sponsor(trial)

2010s

  1. Mar 28, 2014

    Bioverativ Therapeutics Inc. — Earliest FDA Approval

  2. Mar 28, 2014

    Bioverativ Therapeutics Inc. — NDA Organization

Indications

Mechanism of action

Approval history

  • approvedMar 28, 2014

Chemistry & pharmacology

Oral

No

Parenteral

No

Topical

No

Sources

Also known as

  • alprolix
  • alprolix
  • alprolix
  • coagulation factor ix (recombinant), fc fusion protein
  • eftrenonacog alfa
  • eftrenonacog alfa
  • eftrenonacog alfa
  • eftrenonacog alfa
  • eftrenonacog alfa
  • eftrenonacog alfa (genetical recombination)

Clinical trials

NCT IDPhaseStart dateSponsor(s)
NCT03272568Early Phase 1 (Phase 1)Feb 14, 2018Bioverativ Therapeutics Inc., Emory University
NCT03075670Phase 1Mar 7, 2017Novo Nordisk
NCT02234310Phase 3Nov 1, 2014Bioverativ Therapeutics Inc., Swedish Orphan Biovitrum
NCT01440946Phase 3Jun 1, 2012Biogen, Bioverativ Therapeutics Inc., Swedish Orphan Biovitrum
NCT01425723Phase 3Dec 1, 2011Bioverativ Therapeutics Inc.
NCT01027364Phase 3Dec 1, 2009Biogen, Bioverativ Therapeutics Inc., Swedish Orphan Biovitrum
NCT00716716Phase 1Apr 1, 2008Biogen, Bioverativ Therapeutics Inc., Swedish Orphan Biovitrum, Syntonix Pharmaceuticals
Showing 7 of 7 trials
Page 1 / 1

Organizations

Research & Development (6)

OrganizationOrg typeTrialsAs lead sponsorPhasesEarliest year
Bioverativ Therapeutics Inc.For profit6522008
Swedish Orphan BiovitrumFor profit4022008
BiogenFor profit3022008
Emory UniversityAcademic/Hospital1112018
Novo NordiskFor profit1112017
Syntonix PharmaceuticalsFor profit1012008
6 organizations
Page 1 / 1

Marketing (1)

OrganizationOrg typeRelationshipDate
Bioverativ Therapeutics Inc.For profitNDAMar 28, 2014