Leniolisib

Trade name: Joenja

Small moleculeapprovedOrphan Drug FDA

Approved

Mar 24, 2023

Clinical trial activity

9 trials · 10 clinical orgs · 1 marketing orgs

Phase 1
0
Phase 2
7
Phase 3
5
Phase 4
0

Earliest trial started Aug 25, 2015 (NCT02435173)

Timeline

2010s

  1. Jan 1, 2015

    Earliest Phase 2 Sponsor(trial)

  2. Jan 30, 2018

    Orphan Drug Designation

2020s

  1. Jan 1, 2022

    Pharming Group — Earliest Phase 3 Sponsor(trial)

  2. Mar 24, 2023

    Pharming Group — Earliest FDA Approval

  3. Mar 24, 2023

    Pharming Group — Marketing Organization

  4. Mar 24, 2023

    Pharming Group — NDA Secondary Org

  5. Mar 24, 2023

    Pharming Group — NDA Organization

Indications

Mechanism of action

Approval history

  • approvedPriority reviewMar 24, 2023

Chemistry & pharmacology

Loading structure…

SMILES

CCC(=O)N1CC[C@H](Nc2ncnc3c2CN(c2cnc(OC)c(C(F)(F)F)c2)CC3)C1
Mol. weight
450.47 g/mol
Lipinski Ro5
Pass
Rule of 3
No
Chirality
Single Stereoisomer
Inorganic
No
Polymer
No
Delivery
Oral
Availability
Prescription Only

Oral

Yes

Parenteral

No

Topical

No

First in class

Sources

Also known as

  • cdz173
  • cdz173

Clinical trials

NCT IDPhaseStart dateSponsor(s)
NCT06990529Phase 2Apr 29, 2025Aixial Group, Pharming Group
NCT06897358Phase 2Feb 12, 2025Pharming Group, Tufts University
NCT06549114Phase 2Oct 21, 2024National Institutes of Health (NIH), Pharming Group
NCT05693129Phase 3Aug 30, 2023Aixial Group, CMIC Co, Ltd. Japan, Fortrea, LabCorp, Pharming Group
NCT06249997Phase 3Aug 3, 2023Axial Biotech, Inc, CMIC Co, Ltd. Japan, LabCorp, Pharming Group, Tokyo Medical University
NCT05438407Phase 3Aug 31, 2022Aixial Group, CMIC Co, Ltd. Japan, Fortrea, LabCorp, Pharming Group
NCT02859727Phase 2/Phase 3 (Phase 3)Sep 8, 2016Novartis
NCT02775916Phase 2Jun 1, 2016Novartis
NCT02435173Phase 2/Phase 3 (Phase 3)Aug 25, 2015Novartis
Showing 9 of 9 trials
Page 1 / 1

Organizations

Research & Development (10)

OrganizationOrg typeTrialsAs lead sponsorPhasesEarliest year
Pharming GroupFor profit6622022
Aixial GroupFor profit3022022
CMIC Co, Ltd. JapanFor profit3012022
LabCorpFor profit3012022
NovartisFor profit3322015
FortreaFor profit2012022
Axial Biotech, IncFor profit1012023
National Institutes of Health (NIH)Government1012024
Tokyo Medical UniversityAcademic/Hospital1012023
Tufts UniversityAcademic/Hospital1012025
10 organizations
Page 1 / 1

Marketing (3)

OrganizationOrg typeRelationshipDate
Pharming GroupFor profitMKTGMar 24, 2023
Pharming GroupFor profitNDA2Mar 24, 2023
Pharming GroupFor profitNDAMar 24, 2023