autologous bone marrow derived cd34 hspcs electroporated with bcl11a enhancer targeting cas9 ribonucleoprotein

Cell therapyexperimental

Clinical trial activity

1 trials · 1 clinical orgs · 0 marketing orgs

Phase 1
1
Phase 2
0
Phase 3
0
Phase 4
0

Earliest trial started Dec 31, 2024 (NCT06647979)

Timeline

2020s

  1. Jan 1, 2024

    Earliest Phase 1 Sponsor(trial)

Indications

Mechanism of action

  • Stem CellSupplementation

    Stem Cell supplementation

Chemistry & pharmacology

Oral

No

Parenteral

No

Topical

No

Clinical trials

NCT IDPhaseStart dateSponsor(s)
NCT06647979Phase 1Dec 31, 2024Harvard University
Showing 1 of 1 trials
Page 1 / 1

Organizations

Research & Development (1)

OrganizationOrg typeTrialsAs lead sponsorPhasesEarliest year
Harvard UniversityAcademic/Hospital1112024
1 organizations
Page 1 / 1