nerandomilast

Small moleculeapprovedOrphan Drug FDA

Approved

Oct 7, 2025

Clinical trial activity

31 trials · 3 clinical orgs · 1 marketing orgs

Phase 1
23
Phase 2
8
Phase 3
5
Phase 4
0

Earliest trial started May 1, 2012 (NCT01594515)

Timeline

2010s

  1. Jan 1, 2012

    Boehringer Ingelheim — Earliest Phase 1 Sponsor(trial)

2020s

  1. Jan 1, 2020

    Boehringer Ingelheim — Earliest Phase 2 Sponsor(trial)

  2. Jan 1, 2022

    Boehringer Ingelheim — Earliest Phase 3 Sponsor(trial)

  3. Aug 15, 2022

    Orphan Drug Designation

  4. Oct 7, 2025

    Earliest FDA Approval

  5. Oct 7, 2025

    Boehringer Ingelheim — Marketing Organization

Indications

Mechanism of action

Approval history

  • approvedPriority reviewOct 7, 2025

Chemistry & pharmacology

Loading structure…

SMILES

[O-][S+]1CCc2nc(N3CCC(c4ncc(Cl)cn4)CC3)nc(NC3(CO)CCC3)c21
Mol. weight
448.98 g/mol
Lipinski Ro5
Pass
Rule of 3
No
Chirality
Single Stereoisomer
Inorganic
No
Polymer
No

Oral

No

Parenteral

No

Topical

No

Sources

Also known as

  • bi1015550
  • bi 1015550

Clinical trials

NCT IDPhaseStart dateSponsor(s)
NCT07201922Phase 3Jan 23, 2026Boehringer Ingelheim
NCT06806592Phase 3Sep 13, 2025Boehringer Ingelheim
NCT07081932Phase 1Aug 26, 2025Boehringer Ingelheim
NCT07100964Phase 1Aug 11, 2025Boehringer Ingelheim
NCT06241560Phase 2Nov 8, 2024Boehringer Ingelheim
NCT06624072Phase 1Oct 11, 2024Boehringer Ingelheim
NCT06238622Phase 3Jul 10, 2024Boehringer Ingelheim
NCT06408870Phase 1Jun 6, 2024Boehringer Ingelheim
NCT06415045Phase 1May 28, 2024Boehringer Ingelheim
NCT06393127Phase 1May 23, 2024Boehringer Ingelheim
NCT06195072Phase 2Apr 15, 2024Boehringer Ingelheim, Sanofi, Scleroderma Research Foundation, Inc.
NCT06107036Phase 1Feb 26, 2024Boehringer Ingelheim
NCT06139302Phase 1Dec 20, 2023Boehringer Ingelheim
NCT06070610Phase 1Nov 8, 2023Boehringer Ingelheim
NCT05707403Phase 1Feb 14, 2023Boehringer Ingelheim
NCT05718648Phase 1Feb 9, 2023Boehringer Ingelheim
NCT05661344Phase 1Jan 18, 2023Boehringer Ingelheim
NCT05633862Phase 1Jan 13, 2023Boehringer Ingelheim
NCT05550636Phase 1Oct 11, 2022Boehringer Ingelheim
NCT05321082Phase 3Oct 5, 2022Boehringer Ingelheim
Showing 20 of 31 trials
Page 1 / 2

Organizations

Research & Development (3)

OrganizationOrg typeTrialsAs lead sponsorPhasesEarliest year
Boehringer IngelheimFor profit313032012
SanofiFor profit1012024
Scleroderma Research Foundation, Inc.Academic/Hospital1112024
3 organizations
Page 1 / 1

Marketing (1)

OrganizationOrg typeRelationshipDate
Boehringer IngelheimFor profitMKTGOct 7, 2025