pafuramidine maleate

Small moleculeexperimental

Pafuramidine is an experimental drug for the treatment of pneumocystis pneumonia (PCP). In 2006, pafuramidine was given orphan drug status by the US Food and Drug Administration for PCP in patients with HIV/AIDS. Preliminary clinical trials indicated that pafuramide was effective against pneumocystis pneumonia and had the potential for fewer side effects than the standard treatment with trimethoprim/sulfamethoxazole (TMP-SMX). — Wikipedia

Clinical trial activity

5 trials · 13 clinical orgs · 0 marketing orgs

Phase 1
2
Phase 2
4
Phase 3
1
Phase 4
0

Earliest trial started Aug 1, 2001 (NCT00802594)

Timeline

2000s

  1. Jan 1, 2001

    Earliest Phase 2 Sponsor(trial)

  2. Jan 1, 2006

    Earliest Phase 1 Sponsor(trial)

  3. Jan 1, 2006

    Earliest Phase 3 Sponsor(trial)

Indications

Mechanism of action

  • Kinetoplast DNA inhibitor

    Binds to the DNA minor groove in AT sequences of at least four consecutive AT base pairs

Chemistry & pharmacology

Loading structure…

SMILES

CONC(=N)c1ccc(-c2ccc(-c3ccc(C(=N)NOC)cc3)o2)cc1
Mol. weight
364.41 g/mol
Lipinski Ro5
Pass
Rule of 3
No
Chirality
Achiral Molecule
Inorganic
No
Polymer
No

Oral

No

Parenteral

No

Topical

No

Prodrug

Sources

Also known as

  • 2,5-bis(4-amidinophenyl)furan-bis-o-methylamidoxime
  • db289
  • db289
  • db289
  • db 289
  • db-289
  • db289 cpd
  • pafuramidine
  • pafuramidine
  • pafuramidine
  • pafuramidine maleate
  • pafuramidine maleate
  • pafuramidine maleate

Clinical trials

NCT IDPhaseStart dateSponsor(s)
NCT00619346Phase 1Nov 1, 2007Immtech Pharmaceuticals, Inc, Parexel
NCT00408369Phase 1/Phase 2 (Phase 2)Nov 1, 2006Immtech Pharmaceuticals, Inc, Johns Hopkins University
NCT00302341Phase 3May 1, 2006Henry Ford Health System, Immtech Pharmaceuticals, Inc, Medical University of South Carolina, New York University, University of California, San Francisco, University of Chicago, University of Cincinnati, University of North Carolina at Chapel Hill
NCT00803933Phase 2Feb 1, 2003Bill and Melinda Gates Foundation, Immtech Pharmaceuticals, Inc, Programme Nationale de Lutte contre la Trypanosomiase Humaine Africaine
NCT00802594Phase 2Aug 1, 2001Bill and Melinda Gates Foundation, Immtech Pharmaceuticals, Inc, University of Basel
Showing 5 of 5 trials
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Organizations

Research & Development (13)

OrganizationOrg typeTrialsAs lead sponsorPhasesEarliest year
Immtech Pharmaceuticals, IncFor profit5532001
Bill and Melinda Gates FoundationAcademic/Hospital2012001
Henry Ford Health SystemAcademic/Hospital1012006
Johns Hopkins UniversityAcademic/Hospital1012006
Medical University of South CarolinaAcademic/Hospital1012006
New York UniversityAcademic/Hospital1012006
ParexelFor profit1012007
Programme Nationale de Lutte contre la Trypanosomiase Humaine AfricaineAcademic/Hospital1012003
University of BaselAcademic/Hospital1012001
University of California, San FranciscoAcademic/Hospital1012006
University of ChicagoAcademic/Hospital1012006
University of CincinnatiAcademic/Hospital1012006
University of North Carolina at Chapel HillAcademic/Hospital1012006
13 organizations
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