← Mechanisms of action
TTR
SINGLE PROTEINHomo sapiens
Preferred name: Transthyretin ChEMBL ↗
Linked proteins
Drugs acting on this target (14)
| Active Pharmaceutical Ingredient | Mechanism Type ▲ | Approval Status | API Type | Mechanism of Action |
|---|---|---|---|---|
| vutrisiran (Amvuttra) | Activator | approved | Nucleic acid | TTR activator |
| ionis-ttr rx | Agonist | experimental | Nucleic acid | TTR agonist |
| inotersen (tegsedi) | Antagonist | approved | Nucleic acid | TTR antagonist |
| aln-ttr01 | Antisense inhibitor | experimental | Nucleic acid | TTR antisense inhibitor |
| aln-ttrsc04 | Antisense inhibitor | experimental | Nucleic acid | ATTR |
| Eplontersen (Wainua) | Antisense inhibitor | approved | Biological | TTR antisense inhibitor |
| inotersen (tegsedi) | Antisense inhibitor | approved | Nucleic acid | Transthyretin ANTISENSE inhibitor |
| ion 682884 | Antisense inhibitor | experimental | Nucleic acid | TTR antisense inhibitor |
| patisiran (ONPATTRO) | Antisense inhibitor | approved | Nucleic acid | TTR antisense inhibitor |
| at03 | Inhibitor | experimental | Small molecule | TTR inhibitor |
| nnc6019-0001 | Inhibitor | experimental | mAb | TTR inhibitor |
| ntla-2001 | Inhibitor | experimental | Gene therapy | TTR inhibitor |
| Acoramidis (Attruby) | Stabiliser | approved | Small molecule | TTR stabiliser |
| tafamidis (Vyndaqel) | Stabiliser | approved | Small molecule | TTR stabiliser |