← Mechanisms of action
Transthyretin mRNA
NUCLEIC-ACIDHomo sapiens
Drugs acting on this target (5)
| Active Pharmaceutical Ingredient | Mechanism Type ▲ | Approval Status | API Type | Mechanism of Action |
|---|---|---|---|---|
| Eplontersen (Wainua) | Antisense inhibitor | approved | Biological | Transthyretin mRNA antisense inhibitor |
| inotersen (tegsedi) | Antisense inhibitor | approved | Nucleic acid | Transthyretin mRNA antisense inhibitor |
| patisiran (ONPATTRO) | Rnai inhibitor | approved | Nucleic acid | Transthyretin mRNA RNAi inhibitor |
| revusiran | Rnai inhibitor | experimental | Nucleic acid | Transthyretin mRNA RNAi inhibitor |
| vutrisiran (Amvuttra) | Rnai inhibitor | approved | Nucleic acid | Transthyretin mRNA rnai inhibitor |