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Blood Coagulation Disorders, Inherited
Hemorrhagic and thrombotic disorders that occur as a consequence of inherited abnormalities in blood coagulation.
Subtype terms (19)
More specific conditions that are subtypes of Blood Coagulation Disorders, Inherited in the MeSH hierarchy.
- Activated Protein C Resistance
2 drugs approved
- Afibrinogenemia
3 drugs (2 approved, 1 experimental)
- Antithrombin III Deficiency
3 drugs (2 approved, 1 experimental)
- Bernard-Soulier Syndrome
- Factor V Deficiency
- Factor VII Deficiency
8 drugs (3 approved, 5 experimental)
- Factor X Deficiency
1 drug approved
- Factor XI Deficiency
1 drug approved
- Factor XII Deficiency
- Factor XIII Deficiency
1 drug approved
- Gray Platelet Syndrome
- Hemophilia A
104 drugs (53 approved, 51 experimental)
- Hemophilia B
54 drugs (23 approved, 31 experimental)
- Hermanski-Pudlak Syndrome
12 drugs approved
- Hypoprothrombinemias
3 drugs approved
- Protein C Deficiency
1 drug approved
- Thrombasthenia
13 drugs (9 approved, 4 experimental)
- von Willebrand Diseases
17 drugs (8 approved, 9 experimental)
- Wiskott-Aldrich Syndrome
34 drugs (26 approved, 8 experimental)
Drugs by status
Phase 2 trials (1)
Organizations
Organization Involved with Phase 2 Indications (2)