← E76.0

Chapter 4 - Endocrine, nutritional and metabolic diseases (E00-E89)»Metabolic disorders (E70-E88)»Hurler-Scheie syndrome (E76.02)

E76.02

Hurler-Scheie syndrome

Related indications (MeSH) (1)

Mucopolysaccharidosis I27 drugs (17 approved, 10 experimental)

A group of autosomal recessive lysosomal storage disorders caused by mutations in the gene encoding the enzyme, alpha-L-iduronidase (IDUA), required for the degradation of heparan and dermatan sulfates. This leads to abnormal accumulation of these glycosaminoglycans in various tissues causing a wide range of clinical presentations including cognitive and musculoskeletal disorders.