raav1.cmv.hufollistatin344

Gene therapyexperimental

Clinical trial activity

2 trials · 6 clinical orgs · 0 marketing orgs

Phase 1
2
Phase 2
1
Phase 3
0
Phase 4
0

Earliest trial started Jan 1, 2012 (NCT01519349)

Timeline

2010s

  1. Jan 1, 2012

    Earliest Phase 1 Sponsor(trial)

Indications

Mechanism of action

Chemistry & pharmacology

Oral

No

Parenteral

No

Topical

No

Also known as

  • raav1.cmv.hufollistatin344
  • raav1.cmv.hufollistin344

Clinical trials

NCT IDPhaseStart dateSponsor(s)
NCT02354781Phase 1/Phase 2 (Phase 2)Jan 1, 2015Duchenne Alliance, Milo Therapeutics, Ohio State University, Sarepta Therapeutics
NCT01519349Phase 1Jan 1, 2012Ohio State University, Parent Project Muscular Dystrophy, The Myositis Association
Showing 2 of 2 trials
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Organizations

Research & Development (6)

OrganizationOrg typeTrialsAs lead sponsorPhasesEarliest year
Ohio State UniversityAcademic/Hospital2122012
Duchenne AllianceAcademic/Hospital1012015
Milo TherapeuticsFor profit1012015
Parent Project Muscular DystrophyAcademic/Hospital1012012
Sarepta TherapeuticsFor profit1112015
The Myositis AssociationAcademic/Hospital1012012
6 organizations
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