raav1-cmv-gaa
Gene therapyexperimental
Clinical trial activity
1 trials · 2 clinical orgs · 0 marketing orgs
Phase 1
1
Phase 2
1
Phase 3
0
Phase 4
0
Earliest trial started Sep 1, 2010 (NCT00976352)
Timeline
2010s
- Jan 1, 2010
Earliest Phase 1 Sponsor(trial)
Indications
Mechanism of action
- Neutral alpha-glucosidase ABSupplementation
GANAB supplementation
Chemistry & pharmacology
Oral
No
Parenteral
No
Topical
No
Also known as
- raav1-cmv-gaa
Clinical trials
| NCT ID | Phase | Start date | Sponsor(s) |
|---|---|---|---|
| NCT00976352 | Phase 1/Phase 2 (Phase 2) | Sep 1, 2010 | National Heart, Lung, and Blood Institute (NHLBI), University of Florida |
Showing 1 of 1 trials
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Organizations
Research & Development (2)
| Organization | Org type | Trials | As lead sponsor | Phases | Earliest year |
|---|---|---|---|---|---|
| National Heart, Lung, and Blood Institute (NHLBI) | Government | 1 | 0 | 1 | 2010 |
| University of Florida | Academic/Hospital | 1 | 1 | 1 | 2010 |
2 organizations
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