lenti-d drug product
Trade name: Skysona
Gene therapyexperimental
Clinical trial activity
1 trials · 5 clinical orgs · 0 marketing orgs
Phase 1
0
Phase 2
0
Phase 3
1
Phase 4
0
Earliest trial started Aug 1, 2013 (NCT01896102)
Timeline
2010s
- Jan 1, 2013
Earliest Phase 2 Sponsor(trial)
Indications
Studied for
Mechanism of action
- ABCD1Supplementation
ABCD1 supplementation
Chemistry & pharmacology
Oral
No
Parenteral
No
Topical
No
Also known as
- lenti-d drug product
Clinical trials
| NCT ID | Phase | Start date | Sponsor(s) |
|---|---|---|---|
| NCT01896102 | Phase 2/Phase 3 (Phase 3) | Aug 1, 2013 | bluebird bio, Harvard University, University of California, Los Angeles, University of London, University of Minnesota |
Showing 1 of 1 trials
Page 1 / 1
Organizations
Research & Development (5)
| Organization | Org type | Trials | As lead sponsor | Phases | Earliest year |
|---|---|---|---|---|---|
| bluebird bio | For profit | 1 | 1 | 1 | 2013 |
| Harvard University | Academic/Hospital | 1 | 0 | 1 | 2013 |
| University of California, Los Angeles | Academic/Hospital | 1 | 0 | 1 | 2013 |
| University of London | Academic/Hospital | 1 | 0 | 1 | 2013 |
| University of Minnesota | Academic/Hospital | 1 | 0 | 1 | 2013 |
5 organizations
Page 1 / 1