aavrh.10cuarsa
Gene therapyexperimental
Clinical trial activity
1 trials · 3 clinical orgs · 0 marketing orgs
Phase 1
1
Phase 2
1
Phase 3
0
Phase 4
0
Earliest trial started Mar 1, 2013 (NCT01801709)
Timeline
2010s
- Jan 1, 2013
Earliest Phase 1 Sponsor(trial)
Indications
Mechanism of action
- Cerebroside-sulfataseSupplementation
ARSA supplementation
Chemistry & pharmacology
Oral
No
Parenteral
No
Topical
No
Also known as
- aavrh.10cuarsa
Clinical trials
| NCT ID | Phase | Start date | Sponsor(s) |
|---|---|---|---|
| NCT01801709 | Phase 1/Phase 2 (Phase 2) | Mar 1, 2013 | European Leukodystrophy Association, Institut National de la Santé Et de la Recherche Médicale, France, University of Paris |
Showing 1 of 1 trials
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Organizations
Research & Development (3)
| Organization | Org type | Trials | As lead sponsor | Phases | Earliest year |
|---|---|---|---|---|---|
| European Leukodystrophy Association | Academic/Hospital | 1 | 0 | 1 | 2013 |
| Institut National de la Santé Et de la Recherche Médicale, France | Academic/Hospital | 1 | 1 | 1 | 2013 |
| University of Paris | Academic/Hospital | 1 | 0 | 1 | 2013 |
3 organizations
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