aav2cuhcln2
Gene therapyexperimental
Clinical trial activity
1 trials · 2 clinical orgs · 0 marketing orgs
Phase 1
1
Phase 2
0
Phase 3
0
Phase 4
0
Earliest trial started Jun 1, 2004 (NCT00151216)
Timeline
2000s
- Jan 1, 2004
Earliest Phase 1 Sponsor(trial)
Indications
Studied for
Mechanism of action
- Tripeptidyl-peptidase 1Supplementation
supplementation - CLN2
Chemistry & pharmacology
Oral
No
Parenteral
No
Topical
No
Also known as
- aav2cuhcln2
Clinical trials
| NCT ID | Phase | Start date | Sponsor(s) |
|---|---|---|---|
| NCT00151216 | Phase 1 | Jun 1, 2004 | Cornell University, Nathan's Battle Foundation |
Showing 1 of 1 trials
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Organizations
Research & Development (2)
| Organization | Org type | Trials | As lead sponsor | Phases | Earliest year |
|---|---|---|---|---|---|
| Cornell University | Academic/Hospital | 1 | 1 | 1 | 2004 |
| Nathan's Battle Foundation | Academic/Hospital | 1 | 0 | 1 | 2004 |
2 organizations
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