aav-haadc-2

Gene therapyexperimental

Clinical trial activity

5 trials · 8 clinical orgs · 0 marketing orgs

Phase 1
4
Phase 2
2
Phase 3
0
Phase 4
0

Earliest trial started Nov 1, 2004 (NCT00229736)

Timeline

2000s

  1. Jan 1, 2004

    Earliest Phase 1 Sponsor(trial)

2010s

  1. Jan 1, 2016

    Earliest Phase 2 Sponsor(trial)

Indications

Mechanism of action

Chemistry & pharmacology

Oral

No

Parenteral

No

Topical

No

Also known as

  • aav2-haadc
  • aav-haadc-2

Clinical trials

NCT IDPhaseStart dateSponsor(s)
NCT07267065Phase 1Feb 1, 2026Ohio State University
NCT02926066Phase 2Sep 1, 2016National Taiwan University
NCT02852213Phase 1Jul 1, 2016National Institutes of Health (NIH), University of California, San Francisco
NCT02418598Phase 1/Phase 2 (Phase 2)Apr 1, 2015Gene Therapy Research Institution,Co.,Ltd., Jichi Medical University, Takara Bio Inc.
NCT00229736Phase 1Nov 1, 2004Genzyme
Showing 5 of 5 trials
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Organizations

Research & Development (8)

OrganizationOrg typeTrialsAs lead sponsorPhasesEarliest year
Gene Therapy Research Institution,Co.,Ltd.For profit1012015
GenzymeFor profit1112004
Jichi Medical UniversityAcademic/Hospital1112015
National Institutes of Health (NIH)Government1012016
National Taiwan UniversityAcademic/Hospital1112016
Ohio State UniversityAcademic/Hospital1112026
Takara Bio Inc.For profit1012015
University of California, San FranciscoAcademic/Hospital1112016
8 organizations
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