diazoxide choline

Small moleculeapprovedOrphan Drug FDA

Approved

Mar 26, 2025

Clinical trial activity

12 trials · 14 clinical orgs · 1 marketing orgs

Phase 1
4
Phase 2
9
Phase 3
5
Phase 4
0

Earliest trial started May 1, 2008 (NCT00688857)

Timeline

2000s

  1. Jan 1, 2008

    Earliest Phase 1 Sponsor(trial)

  2. Jan 1, 2008

    Earliest Phase 2 Sponsor(trial)

2010s

  1. Jan 1, 2011

    Earliest Phase 3 Sponsor(trial)

  2. May 13, 2014

    Orphan Drug Designation

2020s

  1. Mar 26, 2025

    Earliest FDA Approval

  2. Mar 26, 2025

    Soleno Therapeutics, Inc. — Marketing Organization

Indications

Mechanism of action

Approval history

  • approvedPriority reviewMar 26, 2025

Chemistry & pharmacology

Loading structure…

SMILES

CC1=Nc2ccc(Cl)cc2S(=O)(=O)[N-]1.C[N+](C)(C)CCO
Mol. weight
333.84 g/mol
Lipinski Ro5
Pass
Rule of 3
Yes
Chirality
Achiral Molecule
Inorganic
No
Polymer
No

Oral

No

Parenteral

No

Topical

No

Sources

Also known as

  • diazoxide choline
  • diazoxide choline

Clinical trials

NCT IDPhaseStart dateSponsor(s)
NCT05701774Phase 3Jan 31, 2023Soleno Therapeutics, Inc.
NCT04086810Phase 3Oct 15, 2019Soleno Therapeutics, Inc.
NCT03714373Phase 3Oct 1, 2018Soleno Therapeutics, Inc.
NCT03440814Phase 3May 9, 2018Soleno Therapeutics, Inc.
NCT02893618Phase 2Jul 1, 2017Essentialis, Inc.
NCT02034071Phase 1/Phase 2 (Phase 2)Apr 1, 2014Essentialis, Inc., University of California, Irvine
NCT00973271Phase 3Mar 1, 2011Essentialis, Inc.
NCT00901823Phase 1Mar 1, 2011Essentialis, Inc.
NCT01211860Phase 1Oct 1, 2010Essentialis, Inc., PRACS
NCT01211847Phase 2Oct 1, 2010Essentialis, Inc., Medpace, Inc.
NCT00696475Phase 2Jun 1, 2008Allied Research International, Essentialis, Inc., Frederick C. Smith Clinic, Jacksonville Center for Clinical Research, L-Marc Research Center, Medpace, Inc., Meridien Research, Midwest Institute for Clinical Research, PMG Research, Sterling Research Group, Ltd, TriCities Medical Research
NCT00688857Phase 1May 1, 2008Essentialis, Inc., PRACS
Showing 12 of 12 trials
Page 1 / 1

Organizations

Research & Development (14)

OrganizationOrg typeTrialsAs lead sponsorPhasesEarliest year
Essentialis, Inc.For profit8832008
Soleno Therapeutics, Inc.For profit4412018
Medpace, Inc.For profit2012008
PRACSFor profit2012008
Allied Research InternationalFor profit1012008
Frederick C. Smith ClinicAcademic/Hospital1012008
Jacksonville Center for Clinical ResearchFor profit1012008
L-Marc Research CenterAcademic/Hospital1012008
Meridien ResearchFor profit1012008
Midwest Institute for Clinical ResearchFor profit1012008
PMG ResearchFor profit1012008
Sterling Research Group, LtdFor profit1012008
TriCities Medical ResearchAcademic/Hospital1012008
University of California, IrvineAcademic/Hospital1012014
14 organizations
Page 1 / 1

Marketing (1)

OrganizationOrg typeRelationshipDate
Soleno Therapeutics, Inc.For profitMKTGMar 26, 2025