elivaldogene autotemcel

Trade name: Eli-cel

Cell therapyapprovedOrphan Drug FDABreakthrough Therapy FDA

Approved

Sep 16, 2022

Clinical trial activity

1 trials · 1 clinical orgs · 1 marketing orgs

Phase 1
1
Phase 2
1
Phase 3
0
Phase 4
0

Earliest trial started Mar 24, 2025 (NCT06826196)

Timeline

2010s

  1. Apr 19, 2012

    Orphan Drug Designation

2020s

  1. Sep 16, 2022

    bluebird bio — Earliest FDA Approval

  2. Sep 16, 2022

    bluebird bio — NDA Secondary Org

  3. Sep 16, 2022

    bluebird bio — NDA Organization

  4. Jan 1, 2025

    Earliest Phase 1 Sponsor(trial)

Indications

Mechanism of action

  • ABCD1OTHER

    ABCD1 other

  • ABCD1EXOGENOUS GENE

    ABCD1 exogenous gene

    Gene therapy.

Approval history

  • approvedAcceleratedBreakthroughSep 16, 2022

Chemistry & pharmacology

Chirality
Single Stereoisomer
Inorganic
No
Polymer
No

Oral

No

Parenteral

No

Topical

No

Black box warning

Sources

Clinical trials

NCT IDPhaseStart dateSponsor(s)
NCT06826196Phase 1/Phase 2 (Phase 2)Mar 24, 2025Aldena Therapeutics
Showing 1 of 1 trials
Page 1 / 1

Organizations

Research & Development (1)

OrganizationOrg typeTrialsAs lead sponsorPhasesEarliest year
Aldena TherapeuticsFor profit1112025
1 organizations
Page 1 / 1

Marketing (2)

OrganizationOrg typeRelationshipDate
bluebird bioFor profitNDA2Sep 16, 2022
bluebird bioFor profitNDASep 16, 2022