crd-tmh-001
Gene therapyexperimental
Clinical trial activity
1 trials · 2 clinical orgs · 0 marketing orgs
Phase 1
1
Phase 2
0
Phase 3
0
Phase 4
0
Earliest trial started Aug 31, 2022 (NCT05514249)
Timeline
2020s
- Jan 1, 2022
Earliest Phase 1 Sponsor(trial)
Indications
Studied for
Mechanism of action
- Dystrophin pre-mRNASupplementation
Dystrophin pre-mRNA supplementation
Chemistry & pharmacology
Oral
No
Parenteral
No
Topical
No
Clinical trials
| NCT ID | Phase | Start date | Sponsor(s) |
|---|---|---|---|
| NCT05514249 | Phase 1 | Aug 31, 2022 | Cure Rare Disease, University of Massachusetts |
Showing 1 of 1 trials
Page 1 / 1
Organizations
Research & Development (2)
| Organization | Org type | Trials | As lead sponsor | Phases | Earliest year |
|---|---|---|---|---|---|
| Cure Rare Disease | Academic/Hospital | 1 | 1 | 1 | 2022 |
| University of Massachusetts | Academic/Hospital | 1 | 0 | 1 | 2022 |
2 organizations
Page 1 / 1