autologous cd34+ cells transduced with a lentiviral vector containing the human sgsh gene
Cell therapyexperimental
Clinical trial activity
1 trials · 4 clinical orgs · 0 marketing orgs
Phase 1
1
Phase 2
1
Phase 3
0
Phase 4
0
Earliest trial started Dec 15, 2019 (NCT04201405)
Timeline
2010s
- Jan 1, 2019
Earliest Phase 1 Sponsor(trial)
Indications
Studied for
Mechanism of action
- Unspecified targetTissue restoration
tissue restoration
Chemistry & pharmacology
Oral
No
Parenteral
No
Topical
No
Clinical trials
| NCT ID | Phase | Start date | Sponsor(s) |
|---|---|---|---|
| NCT04201405 | Phase 1/Phase 2 (Phase 2) | Dec 15, 2019 | CTI Clinical Trial and Consulting Services, Orchard Therapeutics Limited, University of London, University of Manchester |
Showing 1 of 1 trials
Page 1 / 1
Organizations
Research & Development (4)
| Organization | Org type | Trials | As lead sponsor | Phases | Earliest year |
|---|---|---|---|---|---|
| CTI Clinical Trial and Consulting Services | For profit | 1 | 0 | 1 | 2019 |
| Orchard Therapeutics Limited | For profit | 1 | 0 | 1 | 2019 |
| University of London | Academic/Hospital | 1 | 0 | 1 | 2019 |
| University of Manchester | Academic/Hospital | 1 | 1 | 1 | 2019 |
4 organizations
Page 1 / 1