dcr-a1at
Nucleic acidexperimental
Clinical trial activity
3 trials · 1 clinical orgs · 0 marketing orgs
Phase 1
1
Phase 2
3
Phase 3
0
Phase 4
0
Earliest trial started Oct 24, 2019 (NCT04174118)
Timeline
Indications
Studied for
Mechanism of action
- Alpha-1-antitrypsinSupplementation
SERPINA1 supplementation
Chemistry & pharmacology
- Chirality
- Single Stereoisomer
- Inorganic
- No
- Polymer
- No
- Multi-specific
- No
Oral
No
Parenteral
No
Topical
No
Sources
- ChEMBLCHEMBL4650380 ↗
Clinical trials
| NCT ID | Phase | Start date | Sponsor(s) |
|---|---|---|---|
| NCT05146882 | Phase 2 | Dec 7, 2021 | Dicerna Pharmaceuticals, Inc. |
| NCT04764448 | Phase 2 | Feb 12, 2021 | Dicerna Pharmaceuticals, Inc. |
| NCT04174118 | Phase 1/Phase 2 (Phase 2) | Oct 24, 2019 | Dicerna Pharmaceuticals, Inc. |
Showing 3 of 3 trials
Page 1 / 1
Organizations
Research & Development (1)
| Organization | Org type | Trials | As lead sponsor | Phases | Earliest year |
|---|---|---|---|---|---|
| Dicerna Pharmaceuticals, Inc. | For profit | 3 | 3 | 1 | 2019 |
1 organizations
Page 1 / 1