volanesorsen sodium

Nucleic acidexperimental

Volanesorsen, sold under the brand name Waylivra, is a triglyceride-reducing drug. It is a second-generation 2'-O-methoxyethyl (2'-MOE) antisense therapeutic oligonucleotide (ASO) that targets the messenger RNA for apolipoprotein C3 (apo-CIII). — Wikipedia

Clinical trial activity

7 trials · 4 clinical orgs · 0 marketing orgs

Phase 1
1
Phase 2
4
Phase 3
4
Phase 4
0

Earliest trial started Aug 1, 2014 (NCT02211209)

Timeline

2010s

  1. Jan 1, 2014

    Earliest Phase 3 Sponsor(trial)

  2. Jan 1, 2015

    Earliest Phase 2 Sponsor(trial)

  3. Jan 1, 2016

    Earliest Phase 1 Sponsor(trial)

Indications

Mechanism of action

Chemistry & pharmacology

Chirality
Single Stereoisomer
Inorganic
No
Polymer
No
Multi-specific
No

Oral

No

Parenteral

No

Topical

No

Sources

Also known as

  • free acid
  • free acid
  • isis 304801
  • isis 304801
  • isis-304801
  • isis-304801
  • volanesorsen
  • volanesorsen
  • volanesorsen
  • volanesorsen sodium
  • volanesorsen sodium

Clinical trials

NCT IDPhaseStart dateSponsor(s)
NCT02910635Phase 1Sep 19, 2016Akcea Therapeutics, Ionis Pharmaceuticals, Inc.
NCT02658175Phase 3Dec 31, 2015Akcea Therapeutics, Ionis Pharmaceuticals, Inc.
NCT02639286Phase 2Dec 17, 2015National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)
NCT02527343Phase 2/Phase 3 (Phase 3)Oct 31, 2015Akcea Therapeutics, Ionis Pharmaceuticals, Inc.
NCT02300233Phase 3Dec 1, 2014Akcea Therapeutics, Ionis Pharmaceuticals, Inc.
NCT02211209Phase 3Aug 1, 2014Akcea Therapeutics, Ionis Pharmaceuticals, Inc.
NCT03544060N/AAkcea Therapeutics, CaligorRx, Inc.
Showing 7 of 7 trials
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Organizations

Research & Development (4)

OrganizationOrg typeTrialsAs lead sponsorPhasesEarliest year
Akcea TherapeuticsFor profit6132014
Ionis Pharmaceuticals, Inc.For profit5522014
CaligorRx, Inc.For profit101
National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)Government1112015
4 organizations
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